Preface: The successful clinical use of viral vectors for human gene therapy |
General principles of retrovirus vector design |
Strategies for retrovirus-based correction of severe, combined immunodeficiency (SCID) |
Retrovirus and lentivirus vector design and methods of cell conditioning |
Analysis of the clonal repertoire of gene corrected cells in gene therapy |
Developing novel lentiviral vectors into clinical products |
Lentivirus vectors in beta-thalassemia |
Gene Therapy for Chronic Granulomatous Disease |
Alternative splicing caused by lentiviral integration in the human genome |
Genotoxicity assay for gene therapy vectors in tumor prone Cdkn2a-/- mice |
Lentiviral Hematopoietic Cell Gene Therapy for X-linked Adrenoleukodystrophy |
Retroviral replicating vectors in cancer |
Adeno-associated virus vectorology, manufacturing and clinical applications |
Gene Delivery To The Retina: From Mouse To Man |
Generation of hairpin-based RNAi vectors for biological and therapeutic application |
Recombinant adeno-associated viral vector reference standards |
NIH oversight of human gene transfer research involving retroviral, lentiviral and adeno-associated virus vectors and the role of the NIH recombinant DNA advisory committee draft |
Regulatory structures for gene therapy medicinal products in the European Union |
Preface: The successful clinical use of viral vectors for human gene therapy |
General principles of retrovirus vector design |
Strategies for retrovirus-based correction of severe, combined immunodeficiency (SCID) |